A Case For Adaptive Design in Clinical Trials

The clinical research industry is in danger of reachingDrug companies, institutes of health, and academic
the point of diminishing returns. By some estimates, itinvestigators are all troubled by the relative dearth of
is already there. The global biopharmaceutical industry,significant pharmaceutical advancement, especially
increasingly battered by escalating R&D costswhen considered against the backdrop of dwindling
and reduced funding, weak ROI, steep regulatorynumbers of medical practitioners and ongoing volatility
challenges, social and political pressure for pricein the healthcare arena. It is not surprising then that
controls, a tarnishing public image and a relentlesslyadaptive trials are coming of age at this particular
competitive marketplace, is dependent on a robustpoint in the history of clinical research, and like any
and impeccable clinical trials industry for the discovery,youth's transition to maturity, that of adaptive design
development, and introduction of new drugs tois at once promising and divisive. Proponents point out
market. However, mounting evidence suggests thatthe increased efficiencies, improved patient outcomes
the traditional clinical trial industry infrastructure isand lower costs of adaptive trials, while opponents
nearing its break point, and the needs of a globalargue statistical inconsistency, potentially troubling
community that is locked in battle with emergenterror rates and regulatory wariness.
disease, pandemic illness, the growth of drug-resistantCertainly, adaptive design is not a panacea. Classically
"super bugs" and exploding - and aging - globaltrained researchers will likely have to change their
populations threaten to outpace theapproach to staff training, trial oversight, regulatory
biopharmaceutical industry's research andcommunication and data capture. And in order to fully
development initiatives. To wit, despite advances indeliver on the promises of adaptive design particular
the speed and precision of data capture and medicalattention must be paid to several key areas, including
communications, clinical trial data are slower to reachethics, finances, regulatory control, methodology,
medical practitioners and health care decision makerslogistics, statistics and technology. However, the use
than in the past. Money poured into clinical trials hasof adaptive design in clinical trials continues to gather
not resulted in faster, better, or more efficient drugsupport from all corners and levels of a complex
development, and data often fall short ofindustry. The case for the use of adaptive designs in
expectations and utility in terms of validity andclinical trials is most simply stated thus: Properly
demonstration of clinically significant efficacy orexecuted adaptive designs enable the delivery of
superiority, compounding opinion that the classicallyvalid outcomes data faster for less cost than
structured clinical trial is not sufficiently flexible toclassically designed clinical trials. Everyone stands to
meet the needs of the current globalgain.
biopharmaceutical community.