Drug Development and the Need For Polymorph Information

New Drugs50-80% of all Drug Substances exist in at least 2
The US Food and Drug Administration (FDA) requirepolymorphic forms
submitters of an Investigational New Drug ApplicationPolymorph A
(INDA - new drug) to submit polymorph information.Polymorph B
Each stage in drug development gets increasingly
The US FDA requires submitters of an Abbreviatedmore complex. After finding a potential hit in a
New Drug Application (ANDA - new generic) thatscreen, the early drug development phase of 'hit to
they must include a polymorphism study in order tolead' follows. This 'lead' drug is then optimised and
demonstrate equivalence.prepared for pre-clinical evaluation. Drug development
In addition, the International Conference onduring the pre-clinical phase is designed to determine
Harmonisation of Technical Requirements ofa drug's safety profile and prepare the drug for use
Pharmaceuticals for Human Use (ICH harmonisedin clinical trials. During drug development, an initial
Tripartite Guideline) ICHQ6A states that the followingscouting polymorph screen is designed to find a
is required: Evidence that polymorphism is or is notstable non-solvated form with good properties. Phase
exhibited by a new drug substance. If polymorphism1 clinical trials are the first time during pharmaceutical
is exhibited, whether the different polymorphic formsdevelopment that the drug is used in humans to test
can affect performance of the drug product, andsafety and tolerability. Larger Clinical Phase 2 studies
what the potential for change is and how it might beassess how well the drug works. This is followed by
controlled.Clinical Phase 3 trials, the most expensive of all, to
Drug Developmentassess drug effectiveness. Phase 3 drug
"Polymorphic forms of a drug substance can havedevelopment work includes a comprehensive
different chemical and physical properties, includingpolymorph screen find as many forms as possible in
melting point, chemical reactivity, apparent solubility,order to exhaustively cover the Intellectual Property
dissolution rate, optical and mechanical properties,space. Continuous monitoring of the polymorphic
vapour pressure, and density. These properties canform is needed throughout the whole drug
have a direct effect on the ability to process and/ordevelopment process in order to ensure consistent
manufacture the drug substance and the drugmanufacture of the specified polymorph
product, as well as on drug product stability,Analytical techniques are powerful tools employed
dissolution, and bioavailability. Thus, polymorphism canduring drug development: X-ray powder diffraction is
affect the quality, safety, and efficacy of the drugused to provide unequivocal proof of polymorphism.
product." [FDA guidelines]. In simple visual terms, theOther methods, including Thermal Analysis; Differential
following scheme shows how to envisageScanning Calorimetry (DSC), Thermal Gravimetric
polymorphism. The Drug Substance is shown as aAnalysis (TGA), Hot-Stage Microscopy (HSM) and
rectangle which can pack together in a crystal inRaman spectroscopy are useful to further
different arrangements. Each separate arrangement ischaracterise polymorphic forms.
a different polymorphic form. It is believed that