Proteomic Discovery, Development - Clinical Submission - From Peptides to Biomarkers

The discovery of peptide biomarkers is happening in- Peptide Biomarker Discovery: 14 months
the midst of many other exciting medical advances- Prototype Assay Development: 5 months
including emerging discoveries in proteomics,- Pre-Validation of Assay: 5 months
personalized medicine, combination products, delivery- Assay Development: 7 months
systems and translational medicine. Peptide biomarker- Clinical Validation: 17 months
discovery is a dynamic area of R&D which is bornClinical Validation includes: preclinical, phase 1, phase 2,
from natural, native physiological and pathologicalphase 3 and phase 4. The number of samples that
processes in biological systems. The field ofmust be collected and tested increase in number and
biomarker discovery and development - identification,size in late phase development. Preclinical POC (Proof
classification, R&D, clinical development phase,of Concept) samples collected and tested are usually
transition and validation is currently under debate. Asmall in number in discovery with around ten samples
number of groups such as NIH (National Institute ofcommon, reaching hundreds of samples in the
Health Biomarker Definitions Working Group, Divisionsvalidation stage, transitioning to thousands of samples
at FDA and other regulatory agencies worldwide areby the time of application to FDA and during
in the process of establishing set criteria forimplementation.
proteomic biomarker development.Regardless of the type, a biomarker must
There are 3 types of Biomarkers:demonstrate, under routine implementation
methodologies and conditions of use, how the
1. Prognostic Biomarkers: capable of providingmarker impacts clinical management of a patient with
information on clinical outcome at the time oflife-threatening or terminal disease, either by
diagnosis, independent of therapyimproving patient outcome or QoL (Quality of Life) or
2. Predictive Biomarkers: capable of providingby lowering cost and time of patient care.
information on the likelihood of response to a givenThe quality, accuracy, reproducibility, consistency and
therapeutic modalityintegrity of data must be of high level and must be
3. Screening Biomarkers: capable of providingquality controlled, processed and assured. Quality
information on clinical diagnosis in the generalmanagement plans, SOPs, WIs, GCP, GLP, GMP and
population.otherwise must be developed and meet compliance
The peptide biomarker developmental phases arequality standards. All plans, procedures and processes
commonly categorized as Discovery, Transition andmust be developed in accordance with FDA
Validation. Estimated time lines for the developmentregulatory requirements, guidance and guidelines for
of a proteomic biomarker (total duration = 48the year of the application and/or implementation.
months) is provided in months: